gene therapy

Cramer, M., Shao, G., Rodino-Klapac, L., Chicoine, L., & Martin, P. (2017). Induction of T-Cell Infiltration and Programmed Death Ligand 2 Expression by Adeno-Associated Virus in Rhesus Macaque Skeletal Muscle and Modulation by Prednisone. Human Gene Therapy, 28(6), 493-509. https://doi.org/10.1089/hum.2016.113 (Original work published 2017)
Xu, R., Jia, Y., Zygmunt, D., Cramer, M., Crowe, K., Shao, G., … Martin, P. (2018). An Isolated Limb Infusion Method Allows for Broad Distribution of rAAVrh74.MCK.GALGT2 to Leg Skeletal Muscles in the Rhesus Macaque. Molecular Therapy. Methods & Clinical Development, 10, 89-104. https://doi.org/10.1016/j.omtm.2018.06.002 (Original work published 2018)
Paul-Heng, M., Leong, M., Cunningham, E., Bunker, D., Bremner, K., Wang, Z., … Sharland, A. (2018). Direct recognition of hepatocyte-expressed MHC class I alloantigens is required for tolerance induction. JCI Insight, 3(15). https://doi.org/10.1172/jci.insight.97500 (Original work published 2018)
Potter, R., Griffin, D., Sondergaard, P., Johnson, R., Pozsgai, E., Heller, K., … Rodino-Klapac, L. (2018). Systemic Delivery of Dysferlin Overlap Vectors Provides Long-Term Gene Expression and Functional Improvement for Dysferlinopathy. Human Gene Therapy, 29(7), 749-762. https://doi.org/10.1089/hum.2017.062 (Original work published 2018)
Flanigan, K., Vetter, T., Simmons, T., Iammarino, M., Frair, E., Rinaldi, F., … Martin, P. (2022). A first-in-human phase I/IIa gene transfer clinical trial for Duchenne muscular dystrophy using rAAVrh74.MCK.GALGT2. Molecular Therapy. Methods & Clinical Development, 27, 47-60. https://doi.org/10.1016/j.omtm.2022.08.009 (Original work published 2022)
Liu, Y., Gong, H., Zhu, J., & Liu, F. (2025). Effective Immune Protection of Mice from Murine Cytomegalovirus Infection by Oral Salmonella-Based Vaccine Expressing Viral M78 Antigen. Vaccines, 13(2). https://doi.org/10.3390/vaccines13020137 (Original work published 2025)