Flanigan, K., Vetter, T., Simmons, T., Iammarino, M., Frair, E., Rinaldi, F., … Martin, P. (2022). A first-in-human phase I/IIa gene transfer clinical trial for Duchenne muscular dystrophy using rAAVrh74.MCK.GALGT2. Molecular Therapy. Methods & Clinical Development, 27, 47-60. https://doi.org/10.1016/j.omtm.2022.08.009 (Original work published 2022)